Approximately 16 boys with Duchenne Muscular Dystrophy (DMD), including several teenagers, are set to benefit from the drug, givinostat. Patients will have to meet certain criteria, including being ...

FRESNO Calif. (KFSN) -- The living room of Zaira De La Cruz's home has been turned into a makeshift hospital room. About seven months after her daughter was born, Zoey was diagnosed with the James ...

AS A PARENT, caregiver, or coach, seeing a kid get pumped about fitness and strength can feel kind of amazing. Especially when you consider that only between 21 to 28 percent of kids ages six to 17 ...

A gene therapy treatment brings hope to 9-year-old Will Leko, diagnosed with Duchenne Muscular Dystrophy, as his family continues to navigate ongoing challenges.

12-year-old Deklan Locke, who has Duchenne muscular dystrophy, uses a power wheelchair and raises awareness about the disease. Duchenne muscular dystrophy is a rare genetic disorder that causes muscle ...

Although it can affect anyone, this lesser-known disorder commonly affects boys and young men. View Entire Post › ...

REDONDO BEACH, Calif. -- Ceri and Rory Devine welcomed their first child, Rhys, into the world three months before COVID-19 shut down the country. It wasn't long before the new parents from Redondo ...

AKRON, Ohio (WJW) – At 14 months old, Marshall Bowling of Millersburg seems a happy little boy, but his journey to this point has not been easy. His challenges started soon after he was born when ...

Novartis' Zolgensma is approved in over 51 countries, and more than 3,700 patients have been treated globally across clinical trials. Most patients in the SMART study maintained motor milestones ...

"Our preliminary findings show that German children with SMA, despite significant physical disability, have surprisingly good subjective HRQoL." – Erik Landfeldt, MSc, PhD Previous studies have found ...

Muscle imaging has evolved into an indispensable tool in the diagnosis and management of muscular dystrophies. Advanced magnetic resonance imaging (MRI) techniques now enable clinicians to quantify ...