After an uneventful pregnancy and birth, Tiffany Green was looking forward to bringing son, Parker James Cameron, home to bond with her and his sisters. But on April 13, a week after Parker’s birth, ...
Findings from St. Jude Children's Research Hospital demonstrate that virtual memory T cells, a specialized group of immune cells, provide nonspecific immunity for infants early in life. The work stems ...
Building on its contributions to newborn screening globally, PerkinElmer’s latest FDA authorized assay enables the simultaneous detection of SMA and SCID SMA is a leading genetic cause of infant death ...
Results from the largest cohort of children who received a gene therapy for a rare immunodeficiency condition have shown the long-term safety and efficacy of the curative treatment, in a study led by ...
“I remember asking the doctor if my daughter was going to die,” said Chelsea Oakley, mother of Cora Oakley, a newborn who was diagnosed with ADA-SCID when she was just seven days old, in April 2017.
Children born without a working immune system due to a rare genetic disorder called Artemis-deficient severe combined immunodeficiency (Artemis-deficient SCID) may be able to lead normal lives thanks ...
A new gene therapy has been shown to be safe and effective in 10 young children who were recently diagnosed with a rare immunodeficiency disorder. This disorder, Artemis-deficient severe combined ...
UCLA researchers are restarting a study to give a gene therapy to kids with an ultra-rare disease. While the one-time therapy is safe and effective, the drug industry has been uninterested. The ...
A new UCLA-led study suggests that advanced genome editing technology could be used as a one-time treatment for the rare and deadly genetic disease CD3 delta severe combined immunodeficiency. The ...
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