Tiny fat bubbles carrying gene therapy have successfully repaired DNA in the lungs and liver of animals with alpha-1 antitrypsin deficiency — a promising leap toward treating humans with this ...

Treatments for bronchiectasis, chronic immune thrombocytopenia, fibromyalgia, Friedreich ataxia, and recurrent respiratory papillomatosis are under review.

Axtell spent 15 hours paddleboarding the gap between Bimini and Lake Worth Beach. Although stormy and hot weather made it ...

The Cystic Fibrosis Foundation has agreed to provide Prime Medicine Inc. an additional investment of up to $24 million to ...

The money raised by the annual event will support the Cystic Fibrosis Foundation and the Miracle League of Whitfield County.

Prime Medicine shares were 9.2% lower, at $3.90, after the company said the Cystic Fibrosis Foundation has agreed to provide it with up to $24 million in additional funding--including a $6 million ...

Boehringer Ingelheim Stiftung announces the winner of the 2025 Heinrich Wieland Prize: Adrian R. Krainer of Cold Spring ...

Today, the Cystic Fibrosis Foundation announced an additional investment of up to $24 million in Prime Medicine to continue ...

Expanded funding builds on the initial agreement to accelerate development of Prime Editors for Cystic Fibrosis (CF) -- ...

Investors say genetic prediction services for embryos, used by Elon Musk and others, are a trust fund for future children.

Then the sunrise was amazing and then you gotta get through the heat and kind of battling through rest of that distance for ...

While NICE recommended the drug for patients with at least one F508del mutation, Vertex struck a reimbursement deal with NHS England for a broader population.