He was diagnosed with Duchenne muscular dystrophy at age 5. "I can remember the day he got diagnosed," said his older sister, ...

Four-year data show preservation of cardiac function, including LVEFSkeletal muscle disease progression continues to slow ...

A North Texas family is sharing a son's journey with Duchenne muscular dystrophy, a rare and progressive muscle-wasting ...

The ouster of the FDA's chief regulator of cell and gene therapies came immediately after a disagreement with her boss over a ...

The Kansas City Chiefs welcomed some special guests to their mandatory minicamp on Tuesday, June 17, and Patrick Mahomes and ...

Sarepta shares face pressure after a second Elevidys-linked death and analyst downgrade over safety concerns and lowered ...

Consequently, Truist Securities expects the launch of two new drugs and the development of the pipeline to help offset ...

Ovarian cancer remains a significant global health challenge, often diagnosed at an advanced stage due to non-specific ...

Robbins LLP reminds stockholders that a class action was filed on behalf of investors who purchased or otherwise ...

During BIO International Convention in Boston USA, the Department of Health – Abu Dhabi (DoH), the regulator of the ...

SynaptixBio announces milestone with selection of candidate drug to treat rare disease H-ABC: Our Bureau, Bengaluru Friday, June 20, 2025, 12:30 Hrs [IST] Oxford-based SynaptixBio ...

The reported dismissal of high-ranking CBER officials Nicole Verdun and Rachael Anatol resurfaced lingering concerns about how gene therapies will be regulated under new FDA leadership.